Elosulfase alpha is a recombinant N-acetylgalactosamine-6-sulfatase enzyme used to treat IVA mucopolysaccharidosis ( Morkio A syndrome ). Got the status of an orphan drug and is approved for use: USA (2014). [one]
| Elosulfase Alpha | |
|---|---|
| Chemical compound | |
| Gross formula | C 5020 H 7588 N 1364 O 1418 S 34 |
| Molar mass | 110.8 kDa |
| Cas | |
| Drugbank | |
| Classification | |
| ATX | |
| Other names | |
| Vimizim (Vimizim) | |
Mechanism of Action
Similar N- acetylgalactosamine-6-sulfatase.
Indications
Mucopolysaccharidosis IVA (Morkio A syndrome). [2]